NCENaional nstitute forHealth and Care ExcellenceNICE贝guidanceOnasemnogeneabeparvovec for treatingpresymptomatic spinalmuscular atrophyHighly specialised technologies guidancePublished:19 April 2023www.nice.org.uk/quidance/hst24NICE 2023.All rights reserved.Subject to Notice of rights (https://www.nice.org.uk/terms-and-conditions#notice-of-rights).